Treatment with Spinraza (nusinersen) can help stabilize or improve motor function in adults with SMA, according to a new ...

Over 95% of babies now diagnosed with SMA are treated with Zolgensma gene therapy, per Daniel Grant, vice president for ...

A higher dose of Spinraza may be more effective than the currently approved dosing schedule for maintaining motor function in ...

Activating a protein called potassium channel Kv2.1 may help improve motor function in spinal muscular atrophy (SMA), according to data from experiments done in mice that point to the protein’s ...

In the last of a series, columnist Sherry Toh shares how she's coping with an intense leg of her journey with chronic pain ...

After facing several damaging storms, columnist Helen Baldwin was delighted to see a daffodil blooming amid the chaos.

Activating a protein called potassium channel Kv2.1 may help improve motor function in SMA, making it a potential SMA ...

This weekend kicked off the MDA annual Clinical & Scientific Conference, bringing together the neuromuscular disease ...

Columnist Sherry Toh thanks the dedicated nurses who've attended to her at various hospitals and at home over the years.

Unearthing an old stuffed animal led columnist Alyssa Silva to recall the memory of realizing how different her childhood was ...

Data from the SAPPHIRE study formed the basis of Scholar Rock's U.S. Food and Drug Administration request to approve ...