The Food and Drug Administration (FDA) has granted Orphan Drug designation to REN001 (Reneo Pharmaceuticals) for the treatment of fatty acid oxidation disorders. REN001 is a selective peroxisome ...

This is a preview. Log in through your library . Abstract Although normal fatty acids (FAs) are degraded via β-oxidation, unusual FAs such as 2-hydroxy (2-OH) FAs and 3-methyl-branched FAs are ...

Proceedings of the National Academy of Sciences of the United States of America, Vol. 115, No. 27 (July 3, 2018), pp. 7039-7044 (6 pages) The mitochondrial trifunctional protein (TFP) catalyzes three ...

PITTSBURGH, July 2, 2020 /PRNewswire/ -- PANTHERx ® Rare Pharmacy announces that it has been selected by Ultragenyx Pharmaceutical as a limited distribution partner for new drug DOJOLVI™ (triheptanoin ...

The process and regulation of FAO. FAO in the TME. SHANNON, CLARE, IRELAND, April 28, 2025 / EINPresswire.com / -- This new review article published in Genes & Diseases sheds light on the pivotal role ...